8-year-old boy first in NY to receive FDA-approved gene therapy for rare inherited blood disorder
by ABC7 New York
ABC7 New York— 8-year-old Yusuf is making history as the first patient in the state of New York to undergo an FDA-approved gene therapy for a rare inherited blood disorder called beta-thalassemia.
CNBC—FDA approves Pfizer’s first gene therapy for rare inherited bleeding disorder. The agency greenlighted the drug, which will be marketed as Beqvez, for adults with moderate to severe hemophilia B.
CBS17.com—Amber Alert issued for 2-year-old, 3-year-old boys last seen in NC, believed to be endangered. SALISBURY, N.C. (WNCN) — The North Carolina Center for Missing Persons has issued an Amber Alert for two young children on Friday night. At...
dailym.ai—Childhood friends of 12-year-old boy who was stabbed to death by homeless man say child killer sentences should be longer as 76-year-old faces parole. Edward Crowley stabbed Diego Pineiro-Villar, 12, around 30 times in March 2000, in a case that shocked the nation and shone a spotlight on failings in the justice system even 20 years ago.